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Advances in Gene Therapy for X-Linked Myotubular Myopathy: Current Progress and Future Challenges

  • Uttaranchal University
  • Jazan University
  • Chitkara University

Research output: Contribution to journalEditorial

2 Scopus citations
Original languageEnglish
Pages (from-to)9-10
Number of pages2
JournalCurrent Gene Therapy
Volume26
Issue number1
DOIs
StatePublished - 2026

Keywords

  • Adeno-associated viruses
  • clinical trials
  • motor function
  • myotubularin
  • neuromuscular diseases
  • respiratory insufficiency

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